The 2nd International Conference on Orphan Drugs and Rare Diseases covers topics such as:
- Medical Aspects and Regulatory issues
- Molecular Genetic Etiology
- Rare Case Studies and Reports
- Genetics and Epigenetics
- Global Rare Diseases and Orphan Drug Market
- Orphan Drugs Clinical Research
- Prevalence, Epidemiology and Forecasting
- Health Policies and Services Organization
- Genomics and Proteomics of Rare Disease
- Pharmacology and Toxicology
- Post-Marketing Safety and Treatment Outcomes
- Gene and Stem Cell Therapy
- Drug Discovery and Developments
- Clinical Research and Developments
- Molecular Genetics
- Translational Science
- Access and Pricing
- Medical Affairs and Regulatory Affairs
- Biomedical Research and Rare Diseases
- Rare Genetic Diseases/Disorders
- Transforming care for rare diseases
- Orphan Drug Therapeutics
- Diagnosis and Challenges
- Revolutionary Changes
- Rare Diseases and Ultra Rare Diseases
- Advancing Research for rare diseases
The 2nd International Conference on Orphan Drugs and Rare Diseases brings together scholars, academics, industry leaders, and enthusiasts
The 2nd International Conference on Orphan Drugs and Rare Diseases will be held in Roma, Italy on 17-19 Mar 2025.