Biomarker for Rare Diseases is a conference that provides an insight on how to identify, test and proof clinical biomarkers in rare disease for regulatory approval.
Biomarker for Rare Diseases covers topics such as:
- Biomarker Validation Plans for Meaningful Conclusions
- Characterization and Identification of Disease Driving Biomarkers
- Therapy Efficacy Demonstration in Preparation for Regulatory Filing
- Clinical Utility of Biomarkers for Rare Disease Drug Development
- Detecting and Diagnosing Disease Earlier by Emerging Techniques and Technologies