The Orphan Drugs for Rare Diseases Summit 2018 covers topics such as:
- Novel drug modalities, assays & models, therapeutic strategies
- Cutting-edge science and tech to enhance rare diseases research, diagnosis and therapeutics
- Emerging approaches for effective, fast, affordable and successful orphan drugs development
- Employee wellbeing & health in relation to office design
- Insights into regulatory, pricing, reimbursement, commercialization, market access for rare disorders drugs
The Orphan Drugs for Rare Diseases Summit 2018 brings together senior attendees with responsibilities in:
- Personalized Medicine
- Drug Discovery & Development
- Experimental Medicine
- Translational Medicine
- Stratified Medicine
- Innovative Medicine
- Cell / Molecular Biology
- Regenerative Medicine
- Diagnostic Development
- Molecular Diagnostics
- Targeted Therapy
- Cell / Gene Therapy
- Genetic Diseases
- Rare & ultra-rare Diseases
- Endocrinology
- Metabolic & Gastrointestinal (GI) disorders
- Cancer / Oncology
- Cardiovascular, pulmonological disorders
- Dermatology, ophthalmology, urology and nephrology Immunology
- Neurology, mental health, neuromuscular and musculoskeletal disorder
- Immunology
- Haematology
- Acute Myeloid Leukemia
- Non-Hodgkin Lymphoma
- Glioma
- Cystic Fibrosis
- Ovarian Cancer
- Pancreatic Cancer
- Duchenne Muscular Dystrophy
- Multiple Myeloma
- Renal Cell Carcinoma
- Graft vs Host Disease
- Market Access
- Clinical Research / Trials / Development
- Alliance Management
- Pricing & Reimbursement
- N-Licensing/Out-Licensing
- Patient Advocacy
- Commercial Development
- Regulatory & Medical Affairs
- Orphan Foundations/Associations
- Health Economics/Outcomes Research (HEOR)
- Big Data
- Bioinformatics
- Digital Health