The 12th European Conference on Rare Diseases and Orphan Products (ECRD 2024) is dedicated to the research and development of public health, social care, support, information, new treatments and healthcare of rare diseases across all European countries including:
- Challenges and experiences in disease specific registries
- Challenges of healthcare pathways
- Challenges of off-label use and access
- How to improve gene testing, genetic counselling and newborn screening at the European level
- How to sustain attractiveness for companies to invest in rare diseases
- The discovery process of a medicinal product from the point of view of industry and regulators
- Opportunities in rare disease collaborative clinical research
- Current landscape of policy development on orphan products and rare disease therapies
The 12th European Conference on Rare Diseases and Orphan Products (ECRD 2024) brings together:
- Academics
- Health care professionals
- Patients representatives
- Payers
- Industry
- Regulators
- Policy makers
The 12th European Conference on Rare Diseases and Orphan Products (ECRD 2024) might be held in 2024.
