Gene Therapy Durability Summit is dedicated to ways for improving efficacy and resulting durability of current gene therapy approaches.
Gene Therapy Durability Summit covers topics such as:
- Definition of durability and the associated regulatory protocol
- Short term immunogenicity and the impact on durability
- Learning from clinical experiences to establish long term durability
- Translational success from models to human trials
- Advancements in vector optimization to maximize durability
- How to overcome long term immunogenicity to improve durability