2nd Rare and Genetic Neurodegenerative Drug Development Summit

The 2nd Rare and Genetic Neurodegenerative Drug Development Summit is dedicated to drug development strategies for rare and genetic neurodegenerative diseases.

Key Topics

• The neurodegenerative drug development investing landscape
• How to tailor your regulatory drug development approach for swift approvals
• Commonalities Between Rare & Genetic Neurodegenerative for a Holistic Overview of Disease
• The potential of precision neurology
• Biomarkers to Understand Neurodegenerative Diseases
• Rare Sub-Groups in Clinical Trials to Inform Trial Design & Enhance Success
• Disease History & Preclinical Packages
• Disease Modelling & Efficacy Proof to Enhance Preclinical Efforts
• Extrapolating Insights From Genetically Defined Populations to Target Common Pathways in Broader Diseases Populations
• Human Genetics – What it Teaches us About Rare Diseases