3rd Rare CNS and Neurodevelopmental Drug Development Summit

The 3rd Rare CNS and Neurodevelopmental Drug Development Summit is dedicated to symptomatic and disease modifying treatments across neurodevelopmental disorders.

The 3rd Rare CNS and Neurodevelopmental Drug Development Summit covers topics such as:

• Specific therapeutic modalities including small molecules, gene therapy, antisense oligonucleotides, gene replacement, stem cell therapy and hybrid strategies
• How to leverage precision medicine to treat rare neurodevelopmental diseases
• The development of translational and quantitative biomarkers to strengthen sensitivity and specificity of outcomes measures
• Symptomatic and disease modifying treatments and how our increased understanding of genetic mechanisms has sharpened our thoughts on targets and disease modifying approaches